U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 00:38:04 GMT 2025
Edited
by admin
on Wed Apr 02 00:38:04 GMT 2025
Nucleic Acid Type OLIGONUCLEOTIDE
Sequence Type COMPLETE
Record UNII
WSP2DHR2BD
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
ISIS-682884
Preferred Name English
EPLONTERSEN SODIUM
USAN  
Official Name English
EPLONTERSEN SODIUM [USAN]
Common Name English
AKCEA-TTR-LRX SODIUM
Code English
ION-682884
Code English
IONIS-TTR-LRX SODIUM
Code English
DNA, d([2'-O-(2-methoxyethyl)]m5rU-sp-[2'-O-(2-methoxyethyl)]m5rC-[2'-O-(2-methoxyethyl)]m5rU-[2'-O-(2-methoxyethyl)]m5rU-[2'-O-(2-methoxyethyl)]rG-Gsp-T-sp-T-sp-A-sp-m5C-sp-A-sp-T-sp-G-sp-A-sp-A-sp-[2'-O-(2-methoxyethyl)]rA-[2'-O-(2-methoxyethyl)]m5rU-[
Common Name English
ION-682884 ICOSASODIUM SALT
Code English
ION-682884 SODIUM
Code English
all-P-ambo-5?-O-{[(6-{5-[(tris{3-[6-(2-acetamido-2-deoxy-?-Dgalactopyranosyloxy)hexylamino]-3-oxopropoxymethyl})methyl]amino-5-oxopentanamido}hexoxy)]phospho}-2?-O-(2-methoxyethyl)-5-methyl-Pthiouridylyl-(3?-O?5?-O)-2?-O-(2-methoxyethyl)-5-methylcytidyly
Common Name English
Eplontersen sodium [WHO-DD]
Common Name English
WAINUA
Brand Name English
Code System Code Type Description
FDA UNII
WSP2DHR2BD
Created by admin on Wed Apr 02 00:38:04 GMT 2025 , Edited by admin on Wed Apr 02 00:38:04 GMT 2025
PRIMARY
NCI_THESAURUS
C174936
Created by admin on Wed Apr 02 00:38:04 GMT 2025 , Edited by admin on Wed Apr 02 00:38:04 GMT 2025
PRIMARY
CAS
2131025-75-5
Created by admin on Wed Apr 02 00:38:04 GMT 2025 , Edited by admin on Wed Apr 02 00:38:04 GMT 2025
PRIMARY
SMS_ID
300000044471
Created by admin on Wed Apr 02 00:38:04 GMT 2025 , Edited by admin on Wed Apr 02 00:38:04 GMT 2025
PRIMARY
USAN
GH-149
Created by admin on Wed Apr 02 00:38:04 GMT 2025 , Edited by admin on Wed Apr 02 00:38:04 GMT 2025
PRIMARY
Sugar Site Range Site Count
2'-O-Methoxyethyl ribose 1_1-1_5;1_16-1_20 10 / 20
Deoxyribose (DNA) 1_6-1_15 10 / 20
Linkage Site Range Site Count
1_3-1_6;1_17-1_18 6 / 19
Sodium Phosporothioate 1_2;1_7-1_16;1_19-1_20 13 / 19
Related Record Type Details
PARENT -> SALT/SOLVATE
TARGET->INHIBITOR OF EXPRESSION
Related Record Type Details
ACTIVE MOIETY