Approval Year
| Substance Class |
Protein
Created
by
admin
on
Edited
Tue Apr 01 21:48:29 GMT 2025
by
admin
on
Tue Apr 01 21:48:29 GMT 2025
|
| Protein Type | TRANSPORTER |
| Protein Sub Type | |
| Sequence Origin | HUMAN |
| Sequence Type | COMPLETE |
| Record UNII |
0189J4XE1H
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Common Name | English | ||
|
Preferred Name | English | ||
|
Common Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
P13569
Created by
admin on Tue Apr 01 21:48:29 GMT 2025 , Edited by admin on Tue Apr 01 21:48:29 GMT 2025
|
PRIMARY | |||
|
0189J4XE1H
Created by
admin on Tue Apr 01 21:48:29 GMT 2025 , Edited by admin on Tue Apr 01 21:48:29 GMT 2025
|
PRIMARY |
| Glycosylation Link Type | Site |
|---|---|
| N | 1_893 |
| N | 1_899 |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
CORRECTOR->TARGET |
Rescues CFTR folding and trafficking to the plasma membrane.
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CORRECTOR->TARGET |
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CORRECTOR->TARGET |
Improve the processing of CFTR
improve the processing and trafficking of CFTR protein to the cell surface
EC50
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COMPLEMENTARY RNA TO REPAIR TARGET MRNA->TARGET |
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CORRECTOR->TARGET |
+ C1 Corrector GLPG2222 (0.15 ?M) in a TECC Assay
EC50
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ACTIVATOR -> TARGET |
Potentiator
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ACTIVATOR -> TARGET |
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CORRECTOR->TARGET | |||
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CORRECTOR->TARGET |
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ACTIVATOR -> TARGET |
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Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| AMINO_ACID_SUBSTITUTION | [1_523] [1_1394] | SITE_SPECIFIC | S-PALMITOYL CYSTEINE | 08WQ73S7SV |
| Name | Property Type | Amount | Referenced Substance | Defining | Parameters | References |
|---|---|---|---|---|---|---|
| MOL_WEIGHT:NUMBER(CALCULATED) | CHEMICAL |
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| Molecular Formula | CHEMICAL |
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